NGGT002
Sponsors
NGGT INC., NGGT (Suzhou) Biotechnology Co., Ltd.
Conditions
Phenylketonurias
Phase 1
AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)
RecruitingNCT06332807
Start: 2025-01-10End: 2030-12-30Target: 12Updated: 2026-08-18
Safety and Efficacy Study of NGGT002 in Adult Patients With Phenylketonuria
RecruitingNCT06687733
Start: 2024-07-16End: 2030-06-11Target: 18Updated: 2026-08-13