N-carbamylglutamate
Sponsors
Mendel Tuchman, Children's Hospital of Philadelphia
Conditions
Carbamyl Phosphate Synthetase DeficiencyInborn Errors of MetabolismMethylmalonic AcidemiaPropionic AcidemiaUrea Cycle Disorders, Inborn
Phase 2
N-Carbamylglutamate (Carbaglu) In The Treatment Of Hyperammonemia
NCT00843921
Start: 2008-08-31End: 2020-06-30Updated: 2020-02-17
Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate
WithdrawnNCT01341379
Start: 2010-12-31End: 2012-08-31Updated: 2014-05-29
Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia
TerminatedNCT01597440
Start: 2012-09-30End: 2015-02-28Updated: 2017-04-26