Myozyme

BIOLOGICAL8 trials

Conditions

Acid Maltase Deficiency DiseaseGlycogen Storage Disease Type IIGlycogen Storage Disease Type II (GSD-II)Glycogen Storage Disease Type II GSD IIGlycogenosis 2Pompe DiseasePompe Disease (Late-onset)Pompe Disease Infantile-Onset

Phase 1

rhGAA in Patients With Infantile-onset Glycogen Storage Disease-II (Pompe Disease)

CompletedNCT00053573

Genzyme, a Sanofi CompanyAcid Maltase Deficiency Disease, Glycogenosis 2, Glycogen Storage Disease Type II +1

Start: 2003-02-28End: 2006-11-30Updated: 2014-02-05

Phase 2

A Study of the Safety and Efficacy of rhGAA in Patients With Infantile-onset Pompe Disease

CompletedNCT00059280

Genzyme, a Sanofi CompanyGlycogen Storage Disease Type II

Start: 2003-04-30End: 2005-09-30Updated: 2014-02-05

Extension Study of Patients With Infantile-Onset Pompe Disease Who Were Previously Enrolled in Protocol AGLU01602

CompletedNCT00125879

Genzyme, a Sanofi CompanyGlycogen Storage Disease Type II

Start: 2005-06-30End: 2006-12-31Updated: 2014-02-06

A Study of rhGAA in Patients With Late-Onset Pompe Disease

CompletedNCT00250939

Genzyme, a Sanofi CompanyAcid Maltase Deficiency Disease, Glycogenosis 2, Glycogen Storage Disease Type II (GSD-II) +1

Start: 2005-02-28End: 2006-11-30Updated: 2014-02-06

Extension Study of Long-term Safety and Efficacy of Myozyme in Patients With Pompe Disease Who Were Previously Enrolled in Genzyme Sponsored Enzyme Replacement Therapy (ERT) Studies

CompletedNCT00763932

Genzyme, a Sanofi CompanyGlycogen Storage Disease Type II, Pompe Disease Infantile-Onset

Start: 2003-04-30End: 2006-07-31Updated: 2014-02-05

Extension Study of Long-term Safety and Efficacy of Myozyme for a Single Patient With Pompe Disease Who Were Previously Enrolled in Genzyme Sponsored ERT Studies.

CompletedNCT00765414

Genzyme, a Sanofi CompanyGlycogen Storage Disease Type II GSD II, Pompe Disease Late-Onset

Start: 2003-04-30End: 2006-08-31Updated: 2014-02-05

Phase 3

Safety and Effectiveness Study of rhGAA in Patients With Advanced Late-Onset Pompe Disease Receiving Respiratory Support

CompletedNCT00268944

Genzyme, a Sanofi CompanyAcid Maltase Deficiency Disease, Glycogenosis 2, Glycogen Storage Disease Type II (GSD-II) +1

Start: 2005-12-31End: 2007-06-30Updated: 2014-02-05

Unknown Phase

Expanded Access Use of Myozyme (Alglucosidase Alfa) in Patients With Late-onset Pompe Disease

CompletedNCT00074932

Genzyme, a Sanofi CompanyGlycogenosis 2, Glycogen Storage Disease Type II