MT-7117 Formulation Code C
Sponsors
Mitsubishi Tanabe Pharma America Inc.
Conditions
Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP)Erythropoietic Protoporphyria or X-Linked Protoporphyria
Phase 3
MT-7117-A-302 Study: A Phase 3, Multicenter, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Efficacy, Safety, and Tolerability of MT-7117 in Adults and Adolescents with Erythropoietic Protoporphyria or X-Linked Protoporphyria
Active, not recruitingCTIS2023-506735-15-00
Start: 2024-04-05Target: 98Updated: 2025-09-17
A Phase 3, Multicenter, Open-label, Long-term, Extension Study to Evaluate Safety and Tolerability of Oral Dersimelagon (MT-7117) in Subjects with Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP)
Active, not recruitingCTIS2024-514466-38-00
Start: 2022-04-19Target: 90Updated: 2025-10-17