Spanish Natural History Study for LAMA2 Muscular Dystrophy
RecruitingNCT06924125
Hospital Universitari Vall d'Hebron Research InstituteCohort Studies, LAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A), Merosin Deficient CMD (Full or Partial) +2
Start: 2021-07-27End: 2030-07-01Target: 100Updated: 2025-04-11
Natural History Study for Patients With Nemaline Myopathy in Spain
RecruitingNCT07488806
Hospital Universitari Vall d'Hebron Research InstituteACTA1, CFL2, Cohort Studies +13
Start: 2026-06-01End: 2032-06-01Target: 100Updated: 2026-03-23