migalastat HCl 20 mg

DRUG2 trials

Sponsors

Amicus Therapeutics

Conditions

Fabry Disease

Phase 3

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

RecruitingNCT06904261

Amicus TherapeuticsFabry Disease

Start: 2026-01-08End: 2028-12-01Target: 8Updated: 2026-09-01

Unknown Phase

Physician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry Disease

Amicus TherapeuticsFabry Disease

Updated: 2025-07-03