IPTACOPAN HYDROCHLORIDE
Sponsors
Novartis Pharma AG
Conditions
C3 Glomerulopathy or idiopathic immune-complex membranoproliferative glomerulonephritisIdiopathic Immune Complex Mediated Membranoproliferative Glomerulonephritis (IC-MPGN)Paroxysmal Nocturnal Hemoglobinuria (PNH)complement 3 glomerulopathy
Phase 3
A multicenter, randomized, double-blind, parallel group, placebo-controlled study to evaluate the efficacy and safety of iptacopan (LNP023) in idiopathic immune complex mediated membranoproliferative glomerulonephritis (IC-MPGN)
RecruitingCTIS2022-502160-20-00
Start: 2023-10-02Target: 41Updated: 2025-12-05
A multicenter, randomized, double-blind, parallel group, placebo-controlled study to evaluate the efficacy and safety of iptacopan (LNP023) in complement 3glomerulopathy
RecruitingCTIS2023-509331-83-00
Start: 2021-07-28Target: 37Updated: 2025-06-25
An open-label, non-randomized extension study to evaluate the long-term efficacy, safety and tolerability of LNP023 in subjects with C3 glomerulopathy or idiopathic immune-complex-membranoproliferative glomerulonephritis
RecruitingCTIS2023-509343-27-00
Start: 2019-10-28Target: 78Updated: 2026-01-27
An open-label, single-arm, multicenter, phase 3 study to assess pharmacokinetics, safety and tolerability of iptacopan in pediatric PNH patients aged 2 to <18 years of age
RecruitingCTIS2024-515926-10-00
Start: 2025-10-28Target: 5Updated: 2025-06-11