Direct Lentiviral Injection Gene Therapy for MLD
Not yet recruitingNCT03725670
Shenzhen Geno-Immune Medical InstituteMetachromatic Leukodystrophy (MLD)
Start: 2027-05-31End: 2028-12-31Target: 10Updated: 2026-09-01
IT and IV Lentiviral Gene Therapy for X-ALD
Not yet recruitingNCT03727555
Shenzhen Geno-Immune Medical InstituteX-linked Adrenoleukodystrophy
Start: 2027-06-01End: 2028-12-31Target: 30Updated: 2026-09-01