HG004

DRUG2 trials

Sponsors

HuidaGene Therapeutics Co., Ltd., Xinhua Hospital, Shanghai Jiao Tong University School of Medicine

Conditions

Inherited Retinal Diseases Caused by RPE65 MutationsLeber Congenital Amaurosis

Early Phase 1

Leber Congenital Amaurosis Inherited Blindness of Gene Therapy Trial(LIGHT)

Active, not recruitingNCT06088992

Xinhua Hospital, Shanghai Jiao Tong University School of MedicineLeber Congenital Amaurosis

Start: 2023-01-10End: 2028-10-30Target: 9Updated: 2024-09-19

Phase 1

Safety and Efficacy Trial of HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR)

RecruitingNCT05906953

HuidaGene Therapeutics Co., Ltd.Inherited Retinal Diseases Caused by RPE65 Mutations, Leber Congenital Amaurosis

Start: 2023-10-31End: 2025-12-31Target: 20Updated: 2024-09-19