Hemlibra 30 mg/mL solution for injection
Sponsors
F. Hoffmann-La Roche AG, Universitair Medisch Centrum Utrecht, HZRM Haemophilie-Zentrum Rhein Main GmbH, Emory University
Conditions
Congenital Haemophilia AHaemophilia AHemophilia AMild or moderate hemophilia A without FVIII inhibitors
Phase 3
A phase IIIb, Multicenter, Open-Label, Single-Arm Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Subcutaneous Emicizumab in Patients From Birth to 12 Months of Age with Hemophilia A without Inhibitors
Active, not recruitingCTIS2023-505964-13-00
Start: 2021-03-09Target: 31Updated: 2025-10-31
Pharmacokinetic-guided dosing of emicizumab in congenital haemophilia A patients – The DosEmi study
RecruitingCTIS2024-515528-35-00
Start: 2022-09-08Target: 135Updated: 2025-12-22
A Multicenter, Open-Label Study to Evaluate the Safety, Efficacy, Pharmacokinetics, and Pharmacodynamics of Emicizumab in Patients with Mild or Moderate Hemophilia A without FVIII Inhibitors
Active, not recruitingCTIS2023-506610-52-00
Start: 2020-06-24Target: 22Updated: 2025-10-31