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Hemlibra 150 mg/mL solution for injection

DRUG7 trials

Sponsors

F. Hoffmann-La Roche AG, Universitair Medisch Centrum Utrecht, HZRM Haemophilie-Zentrum Rhein Main GmbH, Emory University

Conditions

Congenital Haemophilia AHaemophilia AHemophilia AMild or moderate hemophilia A without FVIII inhibitorsSevere or Moderate Hemophilia AType 3 Von Willebrand Disease

Phase 3

A phase IIIb, Multicenter, Open-Label, Single-Arm Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Subcutaneous Emicizumab in Patients From Birth to 12 Months of Age with Hemophilia A without Inhibitors
Active, not recruitingCTIS2023-505964-13-00
F. Hoffmann-La Roche AGHemophilia A
Start: 2021-03-09Target: 31Updated: 2025-10-31
Pharmacokinetic-guided dosing of emicizumab in congenital haemophilia A patients – The DosEmi study
RecruitingCTIS2024-515528-35-00
Universitair Medisch Centrum UtrechtCongenital Haemophilia A
Start: 2022-09-08Target: 135Updated: 2025-12-22
A Multicenter, Open-Label Study to Evaluate the Safety, Efficacy, Pharmacokinetics, and Pharmacodynamics of Emicizumab in Patients with Mild or Moderate Hemophilia A without FVIII Inhibitors
Active, not recruitingCTIS2023-506610-52-00
F. Hoffmann-La Roche AGMild or moderate hemophilia A without FVIII inhibitors
Start: 2020-06-24Target: 22Updated: 2025-10-31
A Phase III, Multicenter, Open-Label Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Emicizumab Prophylaxis in Patients with Type 3 Von Willebrand Disease
RecruitingCTIS2024-515622-80-00
F. Hoffmann-La Roche AGType 3 Von Willebrand Disease
Start: 2025-06-04Target: 47Updated: 2025-06-27
A MULTICENTER, RANDOMIZED, OPEN-LABEL, PHASE III CLINICAL TRIAL TO EVALUATE THE EFFICACY, SAFETY, PHARMACOKINETICS AND PHARMACODYNAMICS OF NXT007 PROPHYLAXIS VERSUS EMICIZUMAB PROPHYLAXIS IN PEOPLE WITH HEMOPHILIA A
Not yet recruitingCTIS2025-522435-33-00
F. Hoffmann-La Roche AGHemophilia A
Target: 43Updated: 2026-06-02

Phase 4