giroctocogene fitelparvovec
Sponsors
Pfizer Inc.
Conditions
hemophilia Asevere to moderately severe hemophilia B (FIX:C ≤ 2%)
Phase 3
C3731003 Phase 3, Open-Label, Single-Arm Study to Evaluate the Efficacy and Safety of PF-07055480 (Recombinant AAV2/6 Human Factor VIII Gene Therapy) in Adult Male Participants with Moderately Severe to Severe Hemophilia A (FVIII:C≤1%)
Active, not recruitingCTIS2024-512075-12-00
Start: 2021-06-14Target: 18Updated: 2026-01-21
C0371017 - A PHASE 3, NON-INVESTIGATIONAL PRODUCT, MULTI COUNTRY COHORT STUDY TO DESCRIBE THE LONG-TERM SAFETY AND EFFECTIVENESS OF A PRIOR SINGLE-DOSE TREATMENT WITH INVESTIGATIVE GIROCTOCOGENE FITELPARVOVEC OR FIDANACOGENE ELAPARVOVEC IN PARTICIPANTS WITH HEMOPHILIA A OR HEMOPHILIA B, RESPECTIVELY
Not yet recruitingCTIS2025-523660-21-00
Target: 7Updated: 2026-04-20