GC301

GENETIC2 trials

Sponsors

GeneCradle Inc

Conditions

Pompe Disease (Late-onset)Pompe Disease Infantile-Onset

Phase 1

Evaluation of the Safety and Efficacy of Infantile-onset Pompe Disease Gene Therapy Drug

Active, not recruitingNCT05793307

GeneCradle IncPompe Disease Infantile-Onset

Start: 2023-06-02End: 2026-12-31Target: 16Updated: 2025-07-03

Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug

RecruitingNCT06391736

GeneCradle IncPompe Disease (Late-onset)

Start: 2024-04-19End: 2026-12-31Target: 33Updated: 2025-07-03