fordadistrogene movaparvovec
Sponsors
Pfizer Inc., Pfizer
Conditions
DUCHENNE MUSCULAR DYSTROPHY (DMD)Duchenne Muscular Dystrophy
Phase 3
A Study to Understand the Long-term Safety and Effects of an Experimental Gene Therapy for Duchenne Muscular Dystrophy.
TerminatedNCT05689164
Start: 2023-03-13End: 2025-09-24Updated: 2025-10-21
C3391003 - A PHASE 3, MULTICENTER, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDY TO EVALUATE THE SAFETY AND EFFICACY OF PF-06939926 FOR THE TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY
Active, not recruitingCTIS2023-508510-42-00
Start: 2025-03-24Target: 48Updated: 2026-01-20