ERT

DRUG3 trials

Sponsors

National Taiwan University Hospital, Amicus Therapeutics, Shionogi

Conditions

Fabry DiseaseGaucher DiseasePompe Disease

Phase 2

An Extension Study of S-606001 in Participants With Late-onset Pompe Disease (LOPD)

Not yet recruitingNCT07750990

ShionogiPompe Disease

Start: 2026-08-31End: 2028-08-31Target: 60Updated: 2026-08-06

Unknown Phase

Miglustat on Gaucher Disease Type IIIB

National Taiwan University HospitalGaucher Disease

Start: 2015-07-31End: 2019-12-31Updated: 2019-03-29

A Study of Patients With Fabry Disease (US Specific)

RecruitingNCT06906367

Amicus TherapeuticsFabry Disease

Start: 2026-02-13End: 2032-06-01Target: 450Updated: 2026-09-09