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Enzyme Replacement Agent

DRUG3 trials

Sponsors

Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau, Hasan Kalyoncu University, AVROBIO

Conditions

Gaucher Disease, Type 3Late Onset Pompe DiseaseMucopolysaccharidosisPompe Disease

Related Papers

Annals of Clinical and Translational Neurology2019-06-1227 citations