DUOC-01
Sponsors
Joanne Kurtzberg, MD
Conditions
AdrenoleukodystrophyAlpha-MannosidosisBatten DiseaseBrain Diseases, Metabolic, InbornLeukodystrophy, Globoid CellLeukodystrophy, MetachromaticMucopolysaccharidosis IINeimann Pick Disease
Phase 1
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
RecruitingNCT02254863
Start: 2014-09-01End: 2027-10-01Target: 40Updated: 2026-09-03
Intrathecal Administration of DUOC-01 in Adults With Primary Progressive Multiple Sclerosis
CompletedNCT04943289
Start: 2021-01-24End: 2025-09-30Updated: 2026-01-08