Delandistrogene moxeparvovec-rokl
Sponsors
Sarepta Therapeutics Inc., F. Hoffmann-La Roche AG
Conditions
Duchenne Muscular DystrophyDuchenne muscular dystrophy (DMD)
Phase 1
Phase 2
Phase 3
A Phase 3, Multinational, Long-Term Follow-Up Study to Evaluate Safety and Efficacy in Subjects Who Have Previously Received SRP-9001 in a Clinical Study
RecruitingCTIS2023-505043-39-00
Start: 2024-05-24Target: 75Updated: 2025-10-13
A Phase 3, Multinational, Randomized, Double-Blind, Placebo-Controlled Systemic Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of SRP-9001 in Non-Ambulatory and Ambulatory Subjects With Duchenne Muscular Dystrophy (ENVISION)
SuspendedCTIS2024-512626-28-00
Start: 2024-03-28Target: 95Updated: 2025-08-18