CS-121
Sponsors
CorrectSequence Therapeutics Co., Ltd, Shanghai Jiao Tong University School of Medicine
Conditions
Familial Chylomicronemia Syndrome (FCS)HyperchylomicronemiaSevere Hypertriglyceridemia (sHTG)
Early Phase 1
CS-121 APOC3 Base Editing in FCS
RecruitingNCT07176923
Start: 2025-10-15End: 2026-12-01Target: 15Updated: 2026-02-11
CS-121 APOC3 Base Editing in Children and Adolescents With Hyperchylomicronemia
RecruitingNCT07371767
Start: 2026-01-26End: 2041-01-31Target: 15Updated: 2026-01-28
CS-121 APOC3 Base Editing in Severe Hypertriglyceridemia
Not yet recruitingNCT07657780
Start: 2026-06-15End: 2028-07-31Target: 15Updated: 2026-06-18