CFTR Modulators
Sponsors
Indiana University, Societe Francaise de la Mucoviscidose, Universidad Europea de Madrid, Children's Hospital Medical Center, Cincinnati, Hospices Civils de Lyon
Conditions
Bone LossCystic FibrosisCystic Fibrosis in ChildrenMuscle Loss
Unknown Phase
CFTR Modulator Effects on Bone and Muscle in Adults With Cystic Fibrosis
Active, not recruitingNCT04206436
Start: 2019-12-18End: 2027-12-31Updated: 2025-10-02
Response to CFTR Modulators in CF Patients Under 18 Years
NCT04301856
Start: 2020-01-01End: 2026-01-01Target: 600Updated: 2021-03-22
Combined Effect of CFTR Protein Modulator Drugs and Exercise in Cystic Fibrosis
WithdrawnNCT04415268
Start: 2020-06-09End: 2021-05-15Updated: 2023-12-11
Testing Drug Efficacy in Cystic Fibrosis Through N-of-1 Trials
RecruitingNCT04580368
Start: 2021-05-01End: 2030-01-31Target: 50Updated: 2026-01-07
Evaluation of the Evolution of Quality of Life in Relation to Naso-sinus Symptomatology Under Treatment With CFTE Modulators in Children Aged 6 to 11 Years With Cystic Fibrosis With Compatible Mutation
CompletedNCT05581056
Start: 2023-03-03End: 2024-09-02Updated: 2025-09-18