BMN 333
Sponsors
Biomarin Pharmaceutical Inc., BioMarin Pharmaceutical
Conditions
Achondroplasia
Phase 2
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
RecruitingNCT07441876
Start: 2026-04-01End: 2029-09-01Target: 160Updated: 2026-05-07
A Multicenter, Randomized, Operationally Seamless Phase 2/3 Study to Evaluate the Efficacy and Safety of BMN 333 versus Vosoritide in Children with Achondroplasia
Not yet recruitingCTIS2025-523811-12-00
Target: 25Updated: 2026-05-05