AT-GTX-501

GENETIC2 trials

Sponsors

Emily de los Reyes

Conditions

Batten DiseaseCLN6Variant Late-Infantile Neuronal Ceroid Lipofuscinosis

Phase 1

Gene Therapy For Children With Variant Late Infantile Neuronal Ceroid Lipofuscinosis 6 (vLINCL6) Disease

CompletedNCT02725580

Emily de los ReyesVariant Late-Infantile Neuronal Ceroid Lipofuscinosis

Start: 2016-05-31End: 2024-10-31Updated: 2025-10-24

Unknown Phase

Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer

Active, not recruitingNCT04273243

Emily de los ReyesBatten Disease, CLN6

Start: 2020-01-24End: 2027-12-31Updated: 2025-10-02