ASP2957

DRUG2 trials

Sponsors

Astellas Gene Therapies Inc., Astellas Gene Therapies

Conditions

X-Linked Myotubular MyopathyX-linked myotubular myopathy

Phase 1

Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators

RecruitingNCT07052929

Astellas Gene TherapiesX-Linked Myotubular Myopathy

Start: 2025-12-15End: 2027-10-31Target: 9Updated: 2026-09-03

A Phase 1/2, Multicenter, Open-label, Dose Escalation and Expansion Clinical Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of ASP2957 in Male Participants with Invasive Ventilator-dependent X-linked Myotubular Myopathy

Not yet recruitingCTIS2025-523213-29-00

Astellas Gene Therapies Inc.X-linked myotubular myopathy

Target: 1Updated: 2026-02-09