ALXN 2040
Sponsors
Alexion Pharmaceuticals Inc.
Conditions
Geographic atrophy (GA) secondary to Age-related Macular Degeneration (AMD)Paroxysmal Nocturnal HemoglobinuriaPatients with Paroxysmal Nocturnal Hemoglobinuria
Phase 2
Phase 3
A Long-term Extension (LTE) Study to Characterize the Safety and Efficacy of Danicopan as an Add-on Therapy to a Complement Component 5 Inhibitor (C5i) in Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) Previously Treated with Danicopan in an Alexion-sponsored Clinical Study.
Active, not recruitingCTIS2023-504867-18-00
Start: 2022-12-05Target: 25Updated: 2025-12-18
A Phase 3 Open-Label Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants with Paroxysmal Nocturnal Hemoglobinuria Who Have Clinically Significant Extravascular Hemolysis
RecruitingCTIS2024-511795-32-00
Start: 2025-02-11Target: 1Updated: 2024-12-16