A Study to Assess Efficacy and Safety of Adimanebart in Adult and Pediatric Participants With DOK7-,MUSK-, AGRN-, or LRP4- Congenital Myasthenic Syndromes (CMS)
Not yet recruitingNCT07746089
argenxCMS, Congenital Myasthenic Syndrome
Start: 2026-09-01End: 2030-10-01Target: 105Updated: 2026-08-04