ABO-101
Sponsors
Arbor Biotechnologies Inc., Abeona Therapeutics, Inc, Arbor Biotechnologies
Conditions
Mucopolysaccharidosis III-BPrimary Hyperoxaluria Type 1 (PH1)
Phase 1
Phase 1/2 Study of ABO-101 in Primary Hyperoxaluria Type 1 (redePHine)
RecruitingNCT06839235
Start: 2025-06-16End: 2043-02-01Target: 23Updated: 2026-02-12
A Phase 1/2 Dose Escalation Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Preliminary Efficacy of ABO-101 in Participants with Primary Hyperoxaluria Type 1 (PH1)
RecruitingCTIS2024-518144-20-00
Start: 2025-09-03Target: 6Updated: 2026-01-26